Orphan Drugs: From Regulatory Issues to Clinical Transition
Faraz Farooq, Alex MacKenzie, Martin Holcik
ISBN: 9781498763073
Vydavatelství: Taylor & Francis
Rok vydání: 2017
Vazba: Hardback
Počet stran: 320
Původní cena: 4 051 Kč
Výstavní cena:
3 443 Kč(t.j. po slevě 15%)
(Cena je uvedena včetně 10% DPH)
Katalogová cena: 115 GBP
Nárok na
dopravu zdarma
Termín dodání na naši pobočku v Brně je přibližně 3-4 týdny.
While drug discovery for common disorders is somewhat standard and based on the large potential markets, the small market for most orphan diseases means that effective therapies are uncommon. With next generation DNA sequencing, the pace of inherited novel rare disease gene identification has increased markedly. Drug discovery for rare diseases is somewhat hampered by a lack of collaboration between academia and industry separating the necessary resources from skills. This volume discusses important aspects of orphan drug development such as regulatory affairs, public industry partnership, bench to bedside using examples of rare diseases, challenges of clinical trials and future directions.